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MaaT Pharma Provides Third Quarter 2024 Business and Financial Results and Announces Management Changes
05 Nov 2024 17:13 GMT
… asset MaaT013 in the treatment of steroid refractory and … continuation of the trial without modification. The trial is a … medical community for MaaT Pharma’s drug candidate MaaT013.
Management Changes … France.
December 5, 2024 – CF&B Midcap Events in …
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Rare diseases patient representatives seek govt intervention to access treatment
05 Nov 2024 16:51 GMT
… of drugs to treat rare diseases, including spinal muscular atrophy (SMA) and cystic fibrosis … a coordinated treatment framework, given the challenges from high drug costs and … the CF therapy, Trikafta, from the American biotech company Vertex Pharmaceuticals. …
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Vertex Tops Q3 Forecast on Strength of Cystic Fibrosis Sales, Raises Full-Year Revenue Guidance
05 Nov 2024 11:54 GMT
Vertex Pharmaceuticals continued its robust … strong demand for its cystic fibrosis therapy Trikafta.
The biotech … continued strong performance” of its cystic fibrosis (CF) therapy Trikafta, sales of … FDA due to release its verdict on the non-opioid pain drug …
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The Effect of Two Somatic-Based Practices Dance and Martial Arts on Irisin, BDNF Levels and Cognitive and Physical Fitness in Older Adults: A Randomized Control Trial
05 Nov 2024 16:00 GMT
… a recent randomized controlled trial (RCT) found decreased … psychiatric diseases or treatments (schizophrenia, bipolar disorder, drug addiction, alcoholism, … could be promising non-pharmacological programs for the … neuroplasticity? J Clin Med. 2020;9(4):1136 …
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Stop abuse of patent monopolies in rare diseases, say patient representatives and treatment activists
05 Nov 2024 14:32 GMT
… access to affordable medication. File image for … representatives and treatment activists have come … cystic fibrosis, patent barriers are similarly overwhelming, with no options for the drug … pharmacy of the developing world by producing and supplying drugs …
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Health groups and patients calls for government interference to make rare disease drugs affordable
05 Nov 2024 14:08 GMT
… , she added.
The drug for CF (CFTR modulators), while … of a child with cystic fibrosis, said that availability of … treatment lifelong.
The 2021 policy also recommended that the Department of Pharmaceuticals … indigenous manufacturing of drugs for rare diseases …
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Raleigh pharma's stock hits record high amid drug launch
05 Nov 2024 14:02 GMT
… the launch of its lead drug.
Verona Pharma (Nasdaq: VRNA) is already … of ensifentrine and the drug glycopyrrolate as a COPD treatment delivered through a … in a Phase 2 trial evaluating ensifentrine in patients with non-cystic fibrosis bronchiectasis.
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An Overview of Commonly Used Natural Alternatives for the Treatment of Androgenetic Alopecia, with Special Emphasis on Rosemary Oil
05 Nov 2024 09:58 GMT
… activity is desirable when treating androgenetic alopecia due to … to the conventional FDA approved medications for the treatment of androgenic … a blinded clinical trial. J Clin Med. 2023;12(2 … Amer KM, Sen P. Pharmacology of rosemary (Rosmarinus officinalis …
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Our children were handed a death sentence when a simple blood test at birth could have saved their lives - by the time doctors took us seriously, it was too late for treatment
05 Nov 2024 09:21 GMT
… serious conditions, among them cystic fibrosis and hypothyroidism (but not … only way you could treat them was a bone marrow … company Orchard Therapeutics developed the drug.
'That means …
Happily Teddi, who began treatment — which is similar to dialysis …
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Vertex Pharma lifts annual revenue forecast on cystic fibrosis treatments strength
04 Nov 2024 21:18 GMT
… 4 (Reuters) - Vertex Pharmaceuticals raised its annual revenue forecast … estimates on demand for its cystic fibrosis (CF) treatments.
The drugmaker now expects … #39;s top-selling CF drug Trikafta rose more than … U.S. approval to treat a rare blood disorder …
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