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Cumberland Pharmaceuticals reports data from trial of ifetroban for DMD
05 Feb 2025 18:44 GMT
… Phase II trial of ifetroban as a potential treatment for Duchenne muscular dystrophy (DMD). … Food and Drug Administration (FDA).
If approved, the drug is expected … critical unmet medical needs.”
Based in Tennessee, Cumberland Pharmaceuticals develops, …
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Entrada gets UK MHRA authorisation to begin Phase I/II trial of DMD treatment
05 Feb 2025 02:38 GMT
… from the UK’s Medicines and Healthcare Products Regulatory … part Phase I/II trial, ELEVATE-44-201, to … Duchenne muscular dystrophy (DMD).
This marks a significant step forward in the potential treatment … ENTR-601-44 for DMD treatment.
Sign up for our …
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Entrada Therapeutics Receives Authorization in the United Kingdom to Initiate ELEVATE-44-201, a Phase 1/2 Multiple Ascending Dose Clinical Study of ENTR-601-44 in Patients Living with Duchenne Muscular Dystrophy
03 Feb 2025 12:00 GMT
… its Clinical Trial of an Investigational Medicinal Product to … 44 for the potential treatment of Duchenne muscular dystrophy (DMD) in patients … adverse events, no drug-related adverse events and … clearance and initiate clinical trials; whether results from …
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Northstrive Biosciences, Inc., a Subsidiary of PMGC Holdings Inc., Reports Positive Updates for Obesity Drug Candidates Targeting Fat Loss and Muscle Preservation used in Combination with GLP-1
04 Feb 2025 13:00 GMT
… model of Duchenne muscular dystrophy), demonstrated … FDA has cleared other myostatin-based therapies to start clinical trials … drug candidates at the exclusive UCLA Obesity Symposium, "Anti-Obesity Treatments … School of Medicine. The presentation …
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OIG Report Seeks Better Oversight, Records for FDA’s Accelerated Approvals
03 Feb 2025 20:23 GMT
… confirmatory trial start before FDA grants … pharmaceutical formulary manager, told the audience. She called for these medications … viable treatments.
Aducanumab
This drug raised … with Duchenne muscular dystrophy.”
Hydroxyprogesterone caproate (HPC)
This drug, …
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How an 1800s French doctor's experiments with electrocuted faces revealed science of real smiles
03 Feb 2025 15:17 GMT
… French physician named Guillaume Duchenne de Boulogne was shocking … pain. Perfect for zapping!
Duchenne would jolt different facial … psychiatric hospital because the medical establishment was all … and it took a French doctor shocking random people…
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Everton stars past and present give brave fan birthday surprise
05 Feb 2025 17:21 GMT
… to remember.
Noah, who has Duchenne muscular dystrophy (DMD), a life-limiting condition … massive milestone for someone with Duchenne muscular dystrophy, so we're super …
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Remembering Philip Weiss, co-founder of adaptive tech start-up for people with disabilities
05 Feb 2025 14:46 GMT
… courageous lifelong battle with Duchenne muscular dystrophy. He died peacefully … managed his own complex medical needs and a team … caregivers, and advised other Duchenne patients online. He … donations to Parent Project Muscular Dystrophy.
Read more about Weiss …
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36 drugs to treat cancer, rare diseases exempted from basic customs duty in Union Budget 2025
01 Feb 2025 11:11 GMT
… far, specified drugs and medicines under PAP run by pharmaceutical companies are fully … access to the promising immunotherapy treatment, mainly due to exorbitant … disease — spinal muscular atrophy or Duchenne muscular dystrophy.
(Edited by Tikli Basu)
Also …
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Minnesotans with disabilities say state’s proposed budget cuts would ‘bring us backward’
05 Feb 2025 13:35 GMT
… wouldn’t be reflected in Medicaid spending data. Terakanambi, who is … describe as cuts. He has Duchenne muscular dystrophy and uses a wheelchair to …