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Santhera Announces Approval In Hong Kong For AGAMREE® (Vamorolone) As A Treatment For Duchenne Muscular Dystrophy
20 Dec 2024 06:28 GMT
… ® for the treatment of Duchenne muscular dystrophy (DMD) in patients aged … Poster presentation. Link . About Duchenne Muscular Dystrophy
Duchenne muscular dystrophy (DMD) is a rare … pivotal study in patients with Duchenne muscular dystrophy (DMD) as an …
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Santhera Announces Approval in Hong Kong for AGAMREE® (Vamorolone) as a Treatment for Duchenne Muscular Dystrophy
20 Dec 2024 06:00 GMT
… ® for the treatment of Duchenne muscular dystrophy (DMD) in patients aged … Poster presentation. Link. About Duchenne Muscular Dystrophy
Duchenne muscular dystrophy (DMD) is a rare … pivotal study in patients with Duchenne muscular dystrophy (DMD) as an …
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Top 5 Duchenne Muscular Dystrophy Content of 2024
20 Dec 2024 00:37 GMT
… year’s top stories on Duchenne muscular dystrophy (DMD) managed care included a … Receives Full FDA Approval for Duchenne Muscular Dystrophy
In March, the FDA approved …
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Ali Abdulwahab Al Mutawa Commercial Co. and Roche Celebrate the First Patient in Kuwait to receive Gene Therapy Treatment for Duchenne Muscular Dystrophy
18 Dec 2024 10:30 GMT
… a new era for treating Duchenne Muscular Dystrophy (DMD) in the country. … groundbreaking step forward in treating Duchenne Muscular Dystrophy. The successful administration of gene … point in the treatment of Duchenne muscular dystrophy, offering new hope for …
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PepGen’s IND for Duchenne Muscular Dystrophy PMO PGN-EDO51 Placed on Clinical Hold by the FDA
18 Dec 2024 02:15 GMT
… oligomer (PMO) intended to treat Duchenne muscular dystrophy (DMD), has been placed on … study of PGN-EDO51 for Duchenne muscular dystrophy. News Release. PepGen Inc. … clinical trial for treatment of Duchenne muscular dystrophy. News Release. PepGen Inc. …
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Sarepta Therapeutics Completes Enrollment in EMERGENE, a Phase 3 Clinical Study of SRP-9003 for the Treatment of Limb-Girdle Muscular Dystrophy Type 2E/R4
18 Dec 2024 13:37 GMT
… complications.
About Limb-girdle Muscular Dystrophy
Limb-girdle muscular dystrophies … hold leadership positions in Duchenne muscular dystrophy (DMD) and limb-girdle … -dystrophin in Children With Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial …
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Study Highlights Trends, Emerging Innovations in DMD Research
22 Dec 2024 19:09 GMT
… hotspots and trends for Duchenne muscular dystrophy: a machine learning bibliometric … . Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, … . Diagnosis and management of Duchenne muscular dystrophy, part 2: respiratory, cardiac …
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Muscular Dystrophy Association and Coalition to Cure Calpain 3 Partner to Fund $300,000 Research Grant for Gene Therapy Development in Limb-Girdle Muscular Dystrophy
17 Dec 2024 13:54 GMT
… (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) and Coalition to … Director of the Center for Duchenne Muscular Dystrophy and member of the … press@mdausa.org. About Muscular Dystrophy Association
Muscular Dystrophy Association (MDA) is the …
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FDA Places Hold on CONNECT2-EDO51, Sevasemten Meets End Point in Becker, Tolebrutinib Gets Breakthrough Therapy Designation
21 Dec 2024 12:22 GMT
… PGN-EDO51 in patients with Duchenne muscular dystrophy (DMD), and will issue an … (CK) among patients with Becker muscular dystrophy. Based on these encouraging findings …
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MRI Biomarker May Signal Early Heart Damage in DMD
20 Dec 2024 21:15 GMT
… cardiac function in boys with Duchenne muscular dystrophy (DMD), even before signs appear … strain in boys with early Duchenne muscular dystrophy cardiomyopathy. Diagnostics (Basel). 2024;14 …