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A Novel COL7A1 Mutation in a Patient With Dystrophic Epidermolysis Bullosa. Successful Treatment With Upadacitinib
20 Jan 2025 18:52 GMT
… email protected]Abstract: Dystrophic epidermolysis bullosa (DEB) is a heterogeneous … Dystrophic epidermolysis bullosa (DEB) is a rare subtype of epidermolysis bullosa (EB … associated with dystrophic epidermolysis bullosa pruriginosa responding effectively …
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Gene Therapy’s Pipeline Has a Steady Flow of More Than 2,000 Candidates
01 Feb 2025 04:15 GMT
… gene therapy for recessive dystrophic epidermolysis bullosa; Neurotech Pharmaceuticals’ NT-501, an …
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Krystal Biotech Provides Update on EMA’s Ongoing Regulatory Review of B-VEC for Dystrophic Epidermolysis Bullosa
09 Dec 2024 21:15 GMT
… ) for the treatment of dystrophic epidermolysis bullosa (DEB) that was scheduled for … for Q2 2025. About Dystrophic Epidermolysis Bullosa (DEB)
DEB is a rare … for the treatment of dystrophic epidermolysis bullosa. The Company is rapidly advancing …
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Pregabalin Significantly Reduces Pain and Itch in Recessive Dystrophic Epidermolysis Bullosa: JAMA
19 Nov 2024 16:57 GMT
… and itch in recessive dystrophic epidermolysis bullosa (RDEB), the most prevalent and … debilitating form of epidermolysis bullosa (EB), a rare skin … and itch in recessive dystrophic epidermolysis bullosa: A randomized crossover trial. JAMA …
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FDA Accepts Abeona Therapeutics' BLA for Epidermolysis Bullosa Gene Therapy Pz-Cel
14 Nov 2024 14:40 GMT
… treatment of recessive dystrophic epidermolysis bullosa. News release. Abeona … patients with Recessive Dystrophic Epidermolysis Bullosa. News release. Abeona Therapeutics … for the Treatment of Dystrophic Epidermolysis Bullosa. News release. Krystal Biotech …
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FDA Accepts Resubmission of Pz-cel Gene Therapy BLA for Epidermolysis Bullosa
13 Nov 2024 20:52 GMT
… for individuals with recessive dystrophic epidermolysis bullosa (RDEB). As part of the … the Treatment of Recessive Dystrophic Epidermolysis Bullosa. Abeona Therapeutics. November 12, 2024 …
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FDA Sets PFUDA Date, Accepts BLA Submission for Pz-cel in Epidermolysis Bullosa
12 Nov 2024 18:34 GMT
… treatment of recessive dystrophic epidermolysis bullosa. News release. Globe … Treatment-of-Recessive-Dystrophic-Epidermolysis-Bullosa.html
Abeona Therapeutics submits … patients with recessive dystrophic epidermolysis bullosa. Abeona Therapeutics Inc. …
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Abeona Therapeutics® Announces FDA Acceptance of BLA Resubmission of Pz-cel for the Treatment of Recessive Dystrophic Epidermolysis Bullosa
12 Nov 2024 12:30 GMT
… new treatment for recessive dystrophic epidermolysis bullosa (RDEB). The FDA has … the treatment of recessive dystrophic epidermolysis bullosa (RDEB), a rare genetic … in development for recessive dystrophic epidermolysis bullosa. The Company’s fully …
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FDA grants BPGbio rare pediatric disease designation for epidermolysis bullosa treatment
31 Oct 2024 22:12 GMT
… BPM31510T for the treatment of epidermolysis bullosa, BPGbio announced in a press … release.
Coinciding with Epidermolysis Bullosa (EB) Awareness Week, the FDA … BPM31510T for the treatment of epidermolysis bullosa. Image: Adobe Stock.
“We are …
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CORRECTING and REPLACING BPGbio Receives FDA Rare Pediatric Disease Designation for its Investigational Treatment for Epidermolysis Bullosa
31 Oct 2024 16:27 GMT
… for its Investigational Treatment for Epidermolysis Bullosa
This marks the company’ … BPM31510T, its investigational treatment for epidermolysis bullosa (EB). This designation coincides … for GBM, pancreatic cancer, and epidermolysis bullosa (EB), as well as …
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