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Expanding Horizons: Researchers Uncover Increasing Number of Genetic Disorders That Can Be Treated Before or at Birth
09 Apr 2025 16:20 GMT
… the risk of genetic disorders. The compiled list of 296 genetic disorders identified through … before birthMass General Brigham researchprenatal genetic disordersprenatal medical geneticsproactive prenatal care approachestreatable fetal …
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Pretzel Therapeutics Announces Publication in Nature Unveiling Discovery of Novel Small Molecule Activators for the Treatment of POLG Disorders and Other Conditions Related to mtDNA Depletion
09 Apr 2025 15:15 GMT
… for the treatment of POLG disorders and other severe conditions linked … breakthrough for patients with POLG disorders, a group of severe and … disorders, the potential applications of these findings may extend beyond rare genetic …
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M6P Therapeutics to Host Virtual KOL Event to Discuss the Lysosomal Storage Disorders Treatment Landscape on April 22, 2025
09 Apr 2025 12:00 GMT
… , autosomal recessive, inherited disorder. He will be joined … genetics, focusing on mitochondrial diseases and lysosomal storage disorders. … and treatment of genetic metabolic diseases. In … therapies for lysosomal storage disorders (LSDs). M6P Therapeutics …
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Tonix Pharmaceuticals and Makana Therapeutics Announce Collaboration Combining Tonix’s Anti-CD40L Monoclonal Antibody (TNX-1500) with Makana’s Genetically Engineered Organs in Preclinical and Clinical Xenotransplantation Studies
09 Apr 2025 11:00 GMT
… rejection of Makana’s genetically engineered pig organs in … central nervous system (CNS) disorders. Tonix’s priority is … reaction and acute stress disorder under a Physician-Initiated … focus on scientifically validated genetics, optimized pig cloning techniques …
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Mouse stem cell study uncovers shared genes for hearing and vision repair
09 Apr 2025 07:47 GMT
… scientists, has identified key genetic barriers to sensory cell regeneration … pathway, a group of interacting genes that act as a ‘ … pathway, a group of interacting genes that act as a “ … on Deafness and Other Communication Disorders, this study provides a …
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New study links mRNA vaccines to GENETIC CHANGES â and not the good kind
09 Apr 2025 01:02 GMT
… proteins, potentially activating pro-inflammatory genes and disrupting immune homeostasis, with … lasting genetic alterations that could potentially lead to cancer and autoimmune disorders … associated with the activation of genes that can promote inflammation …
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Who is Colin Farrell’s eldest son James Farrell? The ‘well-adjusted and happy’ 21-year-old has a rare genetic disorder called Angelman syndrome, and was the reason The Penguin actor quit drinking
07 Apr 2025 21:25 GMT
Colin Farrell may be a critically acclaimed actor in Hollywood, but outside of work, he’s a doting dad to his two sons.
Actor Colin Farrell is the father of two sons. Photo: Xinhua
After winning the title of Best Male Actor in a Limited or Anthology Series …
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New Book Reveals How Genetics Can Treat Anxiety, Reverse Memory Loss, and Transform Psychiatry Forever
08 Apr 2025 18:35 GMT
… evolving landscape of genetic medicine.
Book Details
Title: Cognitive Genetics
Author: Peter … neuromodulators for psychiatric and neurodegenerative disorders through the use of shRNA …
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Only one Colorado hospital offers 'valuable but underused' treatment for rare, genetic cholesterol disorders
08 Apr 2025 12:31 GMT
… addition to familial hypercholesterolemia. The genetic disorders create a high risk for … patients, they generally have significant genetic disorders. So something that they inherited … have a very severe cholesterol disorder that can result in things …
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Opus Genetics Announces One-Month Clinical Data from Pediatric Patient in Phase 1/2 Trial of OPGx-LCA5 Gene Therapy in Inherited Retinal Diseases
08 Apr 2025 12:00 GMT
… a rare and severe genetic disorder that leads to early- … LCA5 gene. About Opus Genetics
Opus Genetics is a clinical-stage … and other treatments for ophthalmic disorders. Our pipeline includes adeno- … that address mutations in genes that cause different forms …