(MENAFN- PR Newswire) SKY-0515 is Skyhawk's investigational small molecule RNA splicing modifier developed through the company's novel RNA-splicing platform. SKY-0515 is designed to reduce both HTT protein and PMS1 protein, an additional key driver …

By the family March 19, 2025: Kerrie Greene was born in Fargo ND, on November 26, 1959, and passed away on March 10 2025, at the age of 65 after a long illness.  A victim of Huntington’s disease, Kerrie had recently resided at the Ferncliff Nursing Home in …

[WEARE, N.H.] The senior advisor to the Pinellas Park, Florida, based Army Reserve Medical Command’s commanding general shared his suicide ideations and his struggles to find resilience in a “Connect to Protect” video conversation. “I had a really big …

The Missouri Chapter of the Huntington's Disease Society of America will host a Team Hope walk Saturday, April 12, at Jackson City Park. Huntington's disease is a fatal genetic disorder that causes a breakdown of nerve cells in the brain, according …

-  LETI-101 has demonstrated therapeutically relevant reductions of mutant huntingtin (HTT) protein, exceeding 80%, while preserving essential wild-type HTT in a clinically relevant Huntington’s disease mouse model -  Administration of LETI-101 in nonhuman …

Medicine scientist using computer while holding test tube with red liquid solution for research ... [+] development. Biochemistry woman with protection glasses and gloves studying lab flaskImage by DC Studio on Freepik A new discovery offers hope for …

To be, or not to be? Hamlet asks this question in Act 3, scene 1 of Shakespeare’s famous tragedy. Hackneyed as the soliloquy has become, Hamlet raises an important query as he waxes existential about the human condition: with the many toils and trials of …

A new UCLA Health study has discovered in mouse models that genes associated with repairing mismatched DNA are critical in eliciting damages to neurons that are most vulnerable in Huntington's disease and triggering downstream pathologies and motor …

Across the recent three months, 8 analysts have shared their insights on Sangamo Therapeutics SGMO, expressing a variety of opinions spanning from bullish to bearish. The following table encapsulates their recent ratings, offering a glimpse into the …

From wetting the bed to acne, we have crunched the numbers on the success rate of every single disability claim. It comes after the Work and Pensions Secretary announced plans to wipe £5billion off the welfare bill, with the bulk of the cuts being made to …