-
uniQure Announces Completion of Enrollment in the First Cohort and Favorable Recommendation from the Independent Data Monitoring Committee for its Phase I/IIa Clinical Trial of AMT-191 for the Treatment of Fabry Disease
03 Feb 2025 12:05 GMT
~ Independent Data Monitoring Committee recommends proceeding with dosing of second cohort after planned safety assessment ~ ~ Company expects to initiate enrollment of second dose cohort in the first quarter of 2025 ~ LEXINGTON, Mass. and AMSTERDAM, Feb. …
-
EQT Life Sciences Leads USD 75 Million Series B In Atalanta Therapeutics, A Biotech Firm Developing Treatments For Epilepsy And Huntington's Disease
28 Jan 2025 13:43 GMT
(MENAFN- PR Newswire)
Atalanta Therapeutics is pioneering RNA interference (RNAi) for the treatment of neurological diseases, having developed a proprietary platform that, for the first time enables RNAi to be deployed as a therapeutic approach throughout …
-
Researchers have made groundbreaking discoveries in the fight against Huntington's disease
23 Jan 2025 04:02 GMT
THIS CONTENT IS BROUGHT TO YOU BY the University of Bergen - read more
This is what protein clumps associated with Huntington's disease look like.
(Image: Markus Miettinene / CBU / University of Bergen)
The findings may pave the way for …
-
Major New Insights Into Huntington's Disease
20 Jan 2025 13:15 GMT
Researchers have made a major breakthrough in our understanding of Huntington's disease. This genetic disorder has long been known to be caused by mutations in the huntingtin gene, which leads to the death of brain cells and neurodegeneration. The …
-
'Unprecedented' brain study brings cure for Huntington's disease a step closer
17 Jan 2025 15:44 GMT
A cure for Huntington’s disease may be a step closer after a study found brain changes linked to the condition could be detected 23 years before a diagnosis.
Symptoms of the inherited disease typically emerge in midlife between the ages of 30 and 50.
…
-
Brain changes in Huntington’s disease decades before diagnosis will guide future prevention trials
17 Jan 2025 10:44 GMT
Subtle changes in the brain, detectable through advanced imaging, blood and spinal fluid analysis, happen approximately twenty years before a clinical motor diagnosis in people with Huntington’s disease, finds a new study led by UCL researchers.
The …
-
Surprise finding sheds light on what causes Huntington's disease, a devastating fatal brain disorder
16 Jan 2025 16:14 GMT
Scientists are unraveling the mystery of what triggers Huntington’s disease, a devastating and fatal hereditary disorder that strikes in the prime of life, causing nerve cells in parts of the brain to break down and die.
The genetic mutation linked to …
-
UC Irvine-Led Team Discovers Potential New Therapeutic Targets for Huntington's Disease
09 Jan 2025 04:51 GMT
Irvine, Calif., Jan. 8, 2025 — A University of California, Irvine-led research team has discovered intricate molecular mechanisms driving the RNA processing defects that lead to Huntington’s disease and link HD with other neurodegenerative disorders such …
-
Potential new therapeutic targets for Huntington's disease
08 Jan 2025 22:11 GMT
A University of California, Irvine-led research team has discovered intricate molecular mechanisms driving the RNA processing defects that lead to Huntington's disease and link HD with other neurodegenerative disorders such as amyotrophic lateral …
-
Wave Life Sciences Announces Submission Of First Clinical Trial Application For WVE-007 (Sirna Targeting INHBE) In Obesity
23 Dec 2024 13:54 GMT
(MENAFN- GlobeNewsWire - Nasdaq) WVE-007 is a novel approach for treating obesity and is designed to silence INHBE to achieve healthy, sustainable weight loss through fat burning, muscle maintenance and the potential for once or twice-annual administration …