-
Neurocrine Biosciences Presents 48-Week Remission Data On Treatment Of Tardive Dyskinesia With INGREZZA® (Valbenazine) Capsules
20 Mar 2025 14:37 GMT
(MENAFN- PR Newswire)
Majority of Participants Reached a Defined Threshold for Remission of Tardive Dyskinesia Regardless of Underlying Psychiatric Disorder
Findings Presented at the 2025 Psychiatry Update Conference
SAN DIEGO, March 20, 2025 / …
-
Rare Neurological Disease Treatment Market to Reach USD 115.8 Billion by 2035, Growing at 9.7% CAGR | Fact.MR Report
18 Mar 2025 11:30 GMT
Rockville, MD, March 18, 2025 (GLOBE NEWSWIRE) -- According to Fact.MR, a market research and competitive intelligence provider, the The global rare neurological disease treatment market was valued at USD 41.8 billion in 2024 and has been forecasted to …
-
Skyhawk Therapeutics Presents At Huntington's Disease Youth Organization HDYO International Congress 2025
15 Mar 2025 11:01 GMT
(MENAFN- PR Newswire)
SKY-0515 is Skyhawk's investigational small molecule RNA splicing modifier developed through the company's novel RNA-splicing platform. SKY-0515 is designed to reduce both HTT protein and PMS1 protein, an additional key driver …
-
ElevateBio Announces Compelling Preclinical Data Demonstrating the Potential of LETI-101 as a Treatment for Huntington's Disease
24 Feb 2025 12:30 GMT
- LETI-101 has demonstrated therapeutically relevant reductions of mutant huntingtin (HTT) protein, exceeding 80%, while preserving essential wild-type HTT in a clinically relevant Huntington’s disease mouse model - Administration of LETI-101 in nonhuman …
-
Four more drugs in keenly watched ALS trial miss the mark
18 Feb 2025 21:31 GMT
Four more experimental drugs for amyotrophic lateral sclerosis (ALS) have failed to hit the primary endpoint in the phase 2/3 HEALEY ALS basket trial, which is trying to accelerate the search for new therapies for the devastating neurodegenerative …
-
Unlocking Huntington's Disease: DNA Repair Protein Could Hold Key To New Treatments
18 Feb 2025 16:47 GMT
Medicine scientist using computer while holding test tube with red liquid solution for research ... [+] development. Biochemistry woman with protection glasses and gloves studying lab flaskImage by DC Studio on Freepik
A new discovery offers hope for …
-
Clinical Trials Market Size to Hit Around USD 186.09 Billion by 2034
13 Feb 2025 13:49 GMT
Ottawa, Feb. 13, 2025 (GLOBE NEWSWIRE) -- The global clinical trials market size was valued at USD 120.98 billion in 2024 and is expected to hit around USD 186.09 billion by 2034 with a CAGR of 4.4% from 2025 to 2034, a study published by Statifacts a …
-
Mystery Solved: New Study Reveals How DNA Repair Genes Play a Major Role in Huntington's Disease
11 Feb 2025 20:41 GMT
A new UCLA Health study has discovered in mouse models that genes associated with repairing mismatched DNA are critical in eliciting damages to neurons that are most vulnerable in Huntington's disease and triggering downstream pathologies and motor …
-
uniQure Announces Completion of Enrollment in the First Cohort and Favorable Recommendation from the Independent Data Monitoring Committee for its Phase I/IIa Clinical Trial of AMT-191 for the Treatment of Fabry Disease
03 Feb 2025 12:05 GMT
~ Independent Data Monitoring Committee recommends proceeding with dosing of second cohort after planned safety assessment ~ ~ Company expects to initiate enrollment of second dose cohort in the first quarter of 2025 ~ LEXINGTON, Mass. and AMSTERDAM, Feb. …
-
PTC Therapeutics and Novartis Partner to Develop Huntington's Disease Treatment
02 Dec 2024 16:10 GMT
Breaking News
Novartis to assume responsibility for PTC518's development, manufacturing and commercialization.
12.02.24
PTC Therapeutics Inc. has signed an exclusive global license and collaboration agreement with Novartis Pharmaceuticals Corporation, …