… for the treatment for metachromatic leukodystrophy (MLD), a rare disease in … , a postdoctoral fellow in the Leukodystrophy Center at CHOP. This study … . “Effective Gene Therapy for Metachromatic Leukodystrophy Achieved with Minimal Lentiviral Genomic …

… therapy approach for treating metachromatic leukodystrophy (MLD), a rare and fatal …

… the rising prevalence of metachromatic leukodystrophy (MLD). MLD is a genetic … Indication: o Treatment of metachromatic leukodystrophy (MLD) o Management of symptoms …

… the disease – called autosomal dominant leukodystrophy (ADLD) – and has significant implications …

… and ultimately fatal type of leukodystrophy. Otherwise known as ION373, the …

… has a rare form of leukodystrophy. It impacts his brain and … a rare form of 4H leukodystrophy. The diagnosis was heartbreaking.  …

… with white matter lesions mimicking leukodystrophy, showed improvement in cognitive … differential diagnosis between MOGAD and leukodystrophy could be challenging. The … usually preserved in patients with leukodystrophies." Tocilizumab was also …

… including adrenoleukodystrophy (ALD), metachromatic leukodystrophy (MLD), Krabbe disease or … for Children with Metachromatic Leukodystrophy. News release. Orchard Therapeutics … with Early-onset Metachromatic Leukodystrophy. News release. Orchard Therapeutics …

… patients with early-onset metachromatic leukodystrophy (MLD). Long-term data from … and Motor Development in Metachromatic Leukodystrophy with up to 12 Years … Therapy for Children with Metachromatic Leukodystrophy. News release. Orchard Therapeutics. March …