… treatment. —Exelixis cancer drug Cabometyx expanded its FDA … Pharmaceuticals developed to treat allergic reactions to insect bites, medications … drug. The FDA approved it in 2000 for treating … muscular dystrophy gene therapy Elevidys, the pharmaceutical …

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WATCH TIME: 4 minutes "This is a very smart move—a combination strategy that addresses both the abnormal and normal protein balance could redefine therapy for OPMD." Oculopharyngeal muscular dystrophy (OPMD) is a rare, late-onset genetic disorder …

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