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FDA leaders kick off rare disease hub to increase cross-center collaboration
16 Oct 2024 18:45 GMT
… CDER, on Wednesday launched a rare disease innovation hub at a
Sign …
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CHOP gets $10 million for tool to transform care for kids with rare diseases
16 Oct 2024 10:21 GMT
… share data on childhood rare diseases, with the goal of … each others’ experiences with rare diseases such as pediatric brain … when it comes to rare diseases, which many doctors don … transform clinical trials of rare diseases in childhood.
When conducting …
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David Cameron opens up on the death of his son aged 6 as he leads push for treatments for rare diseases
16 Oct 2024 08:07 GMT
… to develop more treatments for rare diseases.
Listen to this article
… develop treatments for dozens of rare diseases over the next decade.
… run the Oxford-Harrington Rare Disease Centre because of its … people suffering from a rare disease to see if there …
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Rare Disease Show Episode 18: Understanding Alagille Syndrome with Dr Koutarapu Chandrakant
15 Oct 2024 14:18 GMT
… and why is it a rare disease?
2. What are the key …
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Biotech formed by Pfizer, Roivant eyes treatment for rare diseases
15 Oct 2024 12:36 GMT
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Kerala man contracts murine typhus: What is this rare disease?
15 Oct 2024 10:17 GMT
The oriental rat flea (Xenopsylla cheopsis) is a carrier of murine typhus
| Photo Credit: This media comes from the Centers for Disease Control and Prevention’s Public Health Image Library (PHIL), with identification number #2069 https://commons. …
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Kerala man contracts Murine Typhus: What is this rare disease and who can be infected
15 Oct 2024 09:53 GMT
A 75-year-old man from Kerala has been diagnosed with murine typhus. This is the state's first documented incidence of this unusual bacterial infection. The patient, who had recently travelled to Vietnam and Cambodia, complained of significant physical …
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Local girl who captured community’s heart with humor, bravery while facing rare disease dies at 14
15 Oct 2024 02:44 GMT
… in the face of a rare disease, has died.
Carly Kudzia died …
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Halloween disc golf fundraiser for area youth battling rare disease
15 Oct 2024 01:28 GMT
A young Watervliet girl diagnosed with terminal and incurable Batten Disease is the inspiration behind a fundraising event set for this Saturday, featuring a Haunted Disc Golf Course and Haunted Halloween Trails.
Avaree Dobberstein was diagnosed in January …
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Lundbeck Deepens Neuro, Rare Disease Portfolio With $2.6B Longboard Buy
14 Oct 2024 14:02 GMT
Lundbeck is acquiring neurology and rare diseases specialist Longboard Pharmaceuticals for an … a “cornerstone” of its neuro-rare disease portfolio.
Bexicaserin is being developed …