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Kerala health minister Veena George launched Vishu kaineettam project to support treatment of rare diseases in children
13 Apr 2025 15:51 GMT
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Eating bread daily? Doctor warns it could lead to a rare disease
12 Apr 2025 16:43 GMT
Bread is an integral part of our daily lives. Bread is a quick, convenient breakfast option that pairs well with a variety of toppings like eggs, peanut butter, avocado, or jam. Whole grain or multigrain bread is a healthier choice as it contains more …
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Country music legend battling rare disease. Here’s what to know
12 Apr 2025 15:19 GMT
Country music fans know all too well that opportunities to see legendary singer Alan Jackson live are dwindling.
He took the stage and was great last week at the Grand Ole Opry’s 100th anniversary show, and now he is down to just two regular shows — April …
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Doctor claims eating bread everyday can lead to this rare disease that gets you drunk. What is Auto-Brewery Syndrome?
12 Apr 2025 15:15 GMT
For many people, bread is an everyday staple — especially for breakfast. From buttered toast to jam sandwiches, it remains a go-to item in Indian households. However, health experts are now sounding an alarm about its long-term effects on the body. “Can’t …
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INTERPHEX 2025: The Challenge of Developing Ultra-Rare Disease Treatments
11 Apr 2025 20:11 GMT
… “A Novel Pathway for Ultra-Rare Disease Treatment Development, Commercialization and Access … population sizes,” Katakowski says. “Rare disease is defined as fewer than … drug developers themselves.”
The ultra-rare disease community must work withing the …
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S&D Group Organizes Information Campaign on Rare Diseases
11 Apr 2025 18:19 GMT
… an information campaign on rare diseases. The first of a … often people suffering from rare diseases in Bulgaria do not receive … distribution of drugs for rare diseases. Our group in the … that Bulgarian patients with rare diseases remain deprived of 19 …
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Grey's Anatomy star Eric Dane diagnosed with a rare disease that impairs nervous system
11 Apr 2025 14:46 GMT
Eric Dane, who is famous for playing Dr. Mark Sloan, or "McSteamy," on Grey's Anatomy, has been diagnosed with Amyotrophic Lateral Sclerosis (ALS), a progressive and rare neurological disorder. The 51-year-old actor made the announcement …
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China approves its first gene therapy for rare disease hemophilia B
11 Apr 2025 10:15 GMT
SHANGHAI, April 11 (Xinhua) -- China has approved its first gene therapy for hemophilia B, an inherited bleeding disorder caused by the deficiency of the clotting protein factor IX (FIX).
The National Medical Products Administration has officially approved …
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Odylia Therapeutics drives commitment to rare disease drug development through Rare Disease Day event
10 Apr 2025 20:33 GMT
… expediting drug development for rare diseases, hosted a Rare Disease Day event to … funding and commercialization challenges that rare disease therapies face. “We are … drug development for rare diseases. Every dollar in rare disease research is precious …
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Why Listening to Patients Matters in Rare Disease Research
10 Apr 2025 10:46 GMT
… clinical application.
“People living with rare diseases and their families place great … . “At present, not all hereditary rare diseases are potentially treatable with gene … approach available for treating hereditary rare diseases. “The past decade has seen …