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How Central Virginia family is giving back to kids after losing their loved one to rare disease
07 Feb 2025 20:29 GMT
HENRICO COUNTY, Va. -- A Central Virginia family is helping their son’s memory live on through an annual toy drive for St. Mary’s in honor of his 14th birthday.
The fifth annual Kellan’s Legacy of Love Toy Drive collects new toys for children receiving …
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Tax cut won’t mitigate high prices for cancer, rare diseases medicines, say patient advocacy groups
07 Feb 2025 15:09 GMT
… 36 exorbitantly priced cancer and rare diseases drugs, but patient advocacy groups … public health.
Example is a rare disease drug Risdiplam — over which a … patients as envisaged by the Rare Diseases Policy.
Medicines imported into India …
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‘No One Should Face This’: After Losing Daughter, Dad Ensures No Rare Disease Patient Suffers Alone
06 Feb 2025 21:27 GMT
… APARDO (Asia Pacific Alliance of Rare Disease Organisations) meeting in Manila, … for rare diseases in children, ORDI connects patients with rare disease healthcare … enactment of equitable rare disease health policies.
Putting rare disease advocacy on the …
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AI Drug Repurposing Helps Find Medicine for Rare Disease
06 Feb 2025 09:53 GMT
… Castleman’s disease (iMCD). This rare disease has an especially poor survival … potential treatments for people with rare diseases.
The AI platform, used in …
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AI Technology Paves the Way for Life-Saving Treatments in Rare Disease Research
06 Feb 2025 06:33 GMT
… adalimumab for iMCDadvancements in rare disease therapiesAI in rare disease treatmentartificial intelligence drug discoveryFDA … approved medications for rare diseasesgroundbreaking medical research techniquesidiopathic multicentric …
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Turning aspirations into action for rare disease patients
06 Feb 2025 05:20 GMT
… on her involvement in the rare disease plan at the Belgian health … , ultimately improving outcomes for the rare disease community.”
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AI predicts effective treatment for rare disease using existing medications
06 Feb 2025 03:22 GMT
… 's disease (iMCD). This rare disease has an especially poor survival … potential treatments for people with rare diseases.
The AI platform, used in …
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AI tool helps find life-saving medicine for rare disease
06 Feb 2025 03:10 GMT
… Castleman’s disease (iMCD). This rare disease has an especially poor survival … potential treatments for people with rare diseases.
The AI platform, used in …
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Health Check: Percheron ‘closes the book’ on failed childhood rare disease program
06 Feb 2025 02:25 GMT
Percheron has detailed why its Duchenne muscular dystrophy trial flopped – and why it needs to find a new drug candidate
Imugene’s multiple oncology and inflammation programs aren’t helping its valuation
Impedimed and Micro-X raise funds and Alterity is …
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Cheerleader with rare disease makes miraculous return months after surgery
06 Feb 2025 01:26 GMT
Holy Redeemer junior Eva Kroposky couldn't let an uncurable heart condition keep her off the sidelines. Now she's back to doing what she loves and staying positive.
WILKES-BARRE, Pa. — Holy Redeemer junior, Eva Kroposky, is in her second year …
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