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FDA Grants Regenerative Medicine Advanced Therapy Designation to Laru-Zova for X-Linked Retinitis Pigmentosa
31 Jan 2025 18:18 GMT
… Male Participants With X-linked Retinitis Pigmentosa Caused by RPGR Mutations (DAWN … ) in patients with X-linked retinitis pigmentosa (XLRP). News release. Beacon Therapeutics … Male Subjects With X-linked Retinitis Pigmentosa Caused by RPGR Mutations (SKYLINE …
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Beacon granted FDA Regenerative Medicine Advanced Therapy designation for X-linked retinitis pigmentosa treatment
31 Jan 2025 00:32 GMT
… the treatment of X-linked retinitis pigmentosa (XLRP).
RMAT designation was created …
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FDA RMAT designation for Beacon’s retinitis pigmentosa treatment
29 Jan 2025 10:55 GMT
… -zova, for treating X-linked retinitis pigmentosa (XLRP), a severe, inherited retinal … in XLRP individuals, who express retinitis pigmentosa GTPase regulator (RPGR) gene mutations …
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FDA Grants Regenerative Medicine Advanced Therapy to Laru-Zova for XLRP
31 Jan 2025 15:48 GMT
… the treatment of X-linked retinitis pigmentosa (XLRP).1
Announced by Beacon … caused by mutations in the retinitis pigmentosa regulator (RPGR) gene, accounting for … the treatment of X-linked retinitis pigmentosa. Expert Opin Orphan Drugs. 2018 …
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Promobilia foundation supports KI research on treatments for age-related and inherited visual impairment
31 Jan 2025 15:18 GMT
… inherited retinal degeneration such as retinitis pigmentosa (RP), account for the most …
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Living with blindness, Vickie Kennedy is on a mission to help others adjust
31 Jan 2025 04:41 GMT
… . Vickie Kennedy was diagnosed with Retinitis Pigmentosa, a genetic eye disease commonly …
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Retinal diseases: RNA therapeutics show promise but is India ready?
30 Jan 2025 00:51 GMT
… disease, Leber congenital amaurosis, and retinitis pigmentosa.
Beyond ASOs, researchers are also …
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Local couple helps make Kalaupapa accessible to all
29 Jan 2025 14:39 GMT
… was diagnosed in 1978 with retinitis pigmentosa, commonly known as tunnel vision …
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Sapphire Coast attractions draw in crowds over the 2024 festive season
29 Jan 2025 08:29 GMT
… . Despite going completely blind from Retinitis Pigmentosa at the age of 18 …
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The struggle in the dark: Navigating night blindness
26 Jan 2025 09:49 GMT
… cause of nyctalopia,” Ohito says.
Retinitis Pigmentosa (RP), a genetic disorder, … of retinal degenerative diseases like retinitis pigmentosa. Chronic diseases, such as … into genetic disorders like retinitis pigmentosa and emerging treatments can benefit …