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New hope for those living with Sickle Cell Disease thanks to experimental gene treatment
08 Jun 2024 09:36 GMT
… living with Sickle Cell Disease thanks to a unique new treatment approved by … U.S. Food and Drug Administration.
For the first … babies are born with Sickle Cell Disease.
The condition causes red … unique treatment to cure those symptoms.
In 2023, the FDA …
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Nigerians flock to India for medical treatments, exposing healthcare gaps at home
08 Jun 2024 09:14 GMT
… transplants, bone marrow transplants for sickle cell disease, and treatments for heart diseases.
She … for sickle cell disease, heart diseases because Indians are excellent at cardiovascular treatments.
… healthcare delivery and infrastructure development.
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Significant Fatigue Common in Adult Patients with Sickle Cell Disease
07 Jun 2024 00:06 GMT
Data from a descriptive, prospective study in France revealed that most stable patients with sickle cell disease (SCD), the most prevalent monogenic disorder worldwide, experience significant, and often intense, symptoms of fatigue.1
The study was the …
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Sickle Cell Disease Foundation Announces Real-World Data Initiative, You Are A Marvel, to Transform Sickle Cell Care
06 Jun 2024 17:57 GMT
… and health outcomes beyond medications and treatments alone.”
The YAAM initiative … promote self-agency and the development of quality improvements, products, … #47;yaam
About the Sickle Cell Disease Foundation
The Sickle Cell Disease Foundation (SCDF) was …
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Novel genetic therapies for sickle cell disease and β-thalassemia
05 Jun 2024 19:12 GMT
… gene therapies to be FDA approved for SCD, … gene-editing therapy to treat human disease. Both … therapies for sickle cell disease and β-thalassemias, and their development and … cel gene therapy for sickle cell disease: treatment process evolution and outcomes …
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DoH– Abu Dhabi partners with Pfizer to advance research in sickle cell disease and beyond
05 Jun 2024 04:08 GMT
… prediction, prevention, personalised treatment and access, not … initially focusing on Sickle Cell Disease landscape and exploring … talent supporting research, development and clinical trials. … academia, biotech and pharmaceuticals to unlock opportunities …
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Vertex Presents New Data at the European Cystic Fibrosis Conference Demonstrating Significant Benefits of Treatment with TRIKAFTA®
07 Jun 2024 16:16 GMT
… treatment, projected survival is improving.
Today Vertex CF medicines are treating … their doctor or pharmacist.
Please click here … — cystic fibrosis, sickle cell disease and transfusion-dependent beta … trial results, that data from the company's development …
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Sickle Cell Disease Foundation Announces Research Collaboration with FDA on the Use of Digital Health Technologies to Bridge Health Care Gaps
04 Jun 2024 19:19 GMT
… Drug Administration’s (FDA) Center for Devices and Radiological Health (CDRH) to develop … recent advancements in treatment, individuals living with sickle cell disease continue to face … security of human and veterinary drugs, vaccines, and other biological …
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CRISPR: A promising path to treating blindness
06 Jun 2024 15:01 GMT
… regulators to treat two blood disorders – sickle cell disease and beta- … candidate, EDIT-101, developed by Massachusetts-based Editas … children – showed improvement with treatment. This ‘improvement’ was … ’ previous attempt at treating vision loss with CRISPR …
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Groundbreaking Treatment Makes Way for Sickle Cell Patients
05 Jun 2024 23:07 GMT
… Children’s National Comprehensive Sickle Cell Disease Program, shared his team … approved by the Federal Drug Administration (FDA) in December of … as] the anti-rejection medications put you at higher risk … decision of who receives treatment is largely based on …